#7 The challenge of rare diseases – Christina Ström Möller

By definition, a rare disease is one that only affects a handful
of people in the world. But with more than 300 million people
collectively affected by these conditions and only few approved
treatments available, rare diseases constitute a major unmet
medical need. Christina Ström Möller from Swedish
biopharmaceutical company Sobi walks us through the scientific,
commercial and human challenges of the rare disease landscape.


Tune in to find out:


What drug development, testing and distribution look like
when patients are few and far apart 

Why patient narratives are especially important when
monitoring the safety of rare disease drugs

How patient organisations work to support rare disease
patients and raise awareness of their condition



Want to know more?


Read the stories of patients living with rare diseases on the
Sobi website.

Show your support for Rare Disease Day on 28 February by sharing
campaign materials online with the hashtag #RareDiseaseDay or
joining one of the many events planned around the world.

Rare Disease Day is organised by EURORDIS-Rare Diseases Europe, a
non-profit alliance of rare disease patient organisations from 73
countries.

When assessing the safety of rare disease medicines, also known
as orphan drugs, it is important to include all available sources
of data.

A recent review of orphan drug policies found that several low-
and middle-income countries had developed such policies in the
last decade ­– although disparities between countries with
different income levels still remain.

A survey conducted by EURORDIS in 2020 found that the COVID-19
pandemic exacerbated the many challenges that people living with
a rare disease face.






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